The Role of CD56 During Invasive Aspergillosis

Aspergillus (A.) fumigatus is a species of mold that is found ubiquitously in nature and the inhalation of its spores by healthy adults is a common occurrence having a relatively harmless effect. However, for immunosuppressed patients suffering from hematological malignancies or undergoing hematopoietic stem cell or solid organ transplantation, this species of mold is responsible…

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Regenerative Medicine – Overcoming Regulatory Barriers

Regulatory barriers often inhibit the timely delivery of cutting-edge cellular therapeutics to patients burdened with chronic diseases and disabilities. The Bipartisan Policy Center and Regenerative Medicine Foundation are trying to change this by recommending that Congress support a federally funded registry for regenerative cell therapies. This registry would help share the outcomes of potentially curative…

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Potential of CRISPR-Cas9-based Technology to Treat Congenital Amegakaryocytic Thrombocytopenia (CAMT)

A single mutation in a gene can lead to rare inherited diseases, such as cystic fibrosis, Tay-Sachs, and sickle-cell anemia, and are often difficult to treat and, for most, have no cure. However, with the current advances in CRISPR-Cas9 genome engineering technology, it may be possible to introduce new immunotherapies to treat these and other…

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Treating the side effects of chemotherapy

The human body has many lines of defense against infection, keeping us healthy and free of disease. One immediate line of defense is the innate immune system, which is comprised of white blood cells that are ready to fight against bacterial or fungal infection at birth. One of the most numerous and important cells of…

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How CAR-T cell therapy works

On August 30, 2017, the FDA approved the first US CAR-T cell therapy for the treatment of ALL patients. According to FDA Commissioner Dr. Scott Gottlieb, “We’re entering a new frontier in medical innovation with the ability to reprogram a patient’s own cells to attack a deadly cancer.” Check out this brief video about how…

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A New Approach to Treating Myelodysplastic Syndrome

Myelodysplastic syndrome (MDS) is a group of bone marrow disorders where the bone marrow is incapable of producing healthy mature blood cells. Through a process called hematopoiesis, blood stem cells or hematopoietic stem and progenitor cells (HSPC) within the bone marrow give rise to blood cells, such as white blood cells, platelets, and red blood…

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Integration of Large Transgenes into the Genome of Hematopoietic Primary Cells

RNA-guided CRISPR-Cas9 nuclease is a genome-editing tool that allows researchers to edit parts of the genome by removing, adding, or altering sections of the DNA sequence. CRISPR-Cas9 targets double-stranded DNA using single guided RNA (sgRNA) that shepherds the nuclease to the target DNA sequence. Once at the target, CRISPR-Cas9 creates a double-stranded DNA break. Consequently,…

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Improvements in NIPS Results from Maternal Blood

Chromosome aneuploidies are common genetic defects that can lead to diseases such as Down syndrome. Current methods of aneuploidy testing exist, primarily in the form of chorionic villus sampling or amniocentesis. Although precise, these tests are invasive and may result in intrauterine infection and miscarriage. Recently, fetal genetic material (found in maternal blood) has been…

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